A recent report published by Infinium Global Research on pompe
disease treatment market provides in-depth analysis of segments and
sub-segments in the global as well as regional pompe disease treatment market.
The study also highlights the impact of drivers, restraints, and macro
indicators on the global and regional pompe disease treatment market over the
short term as well as long term. The report is a comprehensive presentation of
trends, forecast and dollar values of global pompe disease treatment market.
According to the report, the global pompe disease treatment market is projected
to grow at a CAGR of 9.0% over the forecast period of 2019-2025.
Pompe disease is a rare neuromuscular disorder that occurs in
children, infants, and adults who inherit a defective gene from their parents.
It is one of the genetic diseases known as lysosomal storage disorders. The
symptoms of Pompe disease are insufficient or missing amounts of an enzyme
called acid alpha-glucosidase (GAA). This enzyme is needed to break down a
complex sugar molecule into glucose.it is a simple sugar that our bodies use
for energy. Pompe disease is a progressive disease that gets worse over time.
This disease causes progressive muscle weakness and often leads to breathing
problems. It is also considered as a metabolic muscle disease. It is similar to
other neuromuscular disorders such as muscular dystrophies.
The growing special regulatory drug designations for orphan drugs
and increasing research activities performed to find an effective treatment for
the disease are driving the pompe disease treatment market. Further Enzyme
replacement therapies and growing developments in gene therapy also provide
significant growth to the market. However, inflated costs associated with Pompe
disease therapy is hindering the growth of the market. Moreover, emerging
immunotherapeutic approaches for pompe disease provide growth opportunities for
pompe disease treatment market
Geographically, the pompe disease treatment market is segmented
into North America, Europe, the Asia-Pacific, and the Row. North America is the
largest region for global pompe disease treatment market. The occurrence of the
disease is 1 out of 40,000 births in the U.S. drug and food
administration has approved an enzyme replacement therapy Lumizyme® is used for
patients older than 8 years of age. Whereas Myozyme® for the infantile-onset of
Pompe disease suffering patients of less than 8 years old. Asia-Pacific is
expected to grow with healthy CAGR owing to healthcare facilities and
increasing awareness among patients regarding rare disorders.
The report on global pompe disease treatment market covers
segments such as therapy type, molecule type, route of administration, and
dosage forms. On the basis of therapy type, the sub-markets include enzyme
replacement therapy, and substrate reduction therapy. On the basis of molecule
type, the sub-markets include biologics, and small molecules. On the basis of
route of administration, the sub-markets include oral, and parenteral. On the
basis of dosage forms, the sub-markets include solid, and liquid.
The report provides profiles of the companies in the market such
as BioMarin Pharmaceutical, Amicus Therapeutics, Genzyme company, Oxyrane,
Audentes Therapeutics, Sangamo BioSciences, EpiVax, and Valerion Therapeutics.
The report provides deep insights into the demand forecasts,
market trends, and micro and macro indicators. In addition, this report
provides insights into the factors that are driving and restraining the growth
in this market. Moreover, The IGR-Growth Matrix analysis given in the report
brings an insight into the investment areas that existing or new market players
can consider. The report provides insights into the market using analytical
tools such as Porter's five forces analysis and DRO analysis of pompe disease
treatment market. Moreover, the study highlights current market trends and provides
forecast from 2019-2025. We also have highlighted future trends in the market
that will affect the demand during the forecast period. Moreover, the
competitive analysis given in each regional market brings an insight into the
market share of the leading players.